NIH researchers discovered a new form of ALS that begins in childhood. The study linked the disease to a gene called SPLTC1. As part of…
Posts published in “Gene Therapy”
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The CRISPR-based gene editor, C-to-G Base Editor (CGBE), opens up treatment avenues for up to 40 percent of genetic disorders caused by single-nucleotide mutations. A…
A piece of the tumor was made completely transparent and scanned in 3D with a special microscope. The components labeled with fluorescent colors were rendered…
Study shows treatment developed by international team restored immune function in more than 95% of patients in three clinical trials. An experimental form of gene…
Professor Jose Polo in front of images of the iBlastoids. Credit: Monash University For first time, fibroblast-derived model of early embryo will allow extensive study…
Electron microscopy image of DNA origami rotor arms, which are the faint orange “L’s” attached to the purple tracking particles. Credit: Image courtesy of Julene…
Tian’s research reveals a novel winner-takes-all resource competition between synthetic gene circuits within one host cell. Credit: Graphic created by Xiaojun Tian/ASU Division of synthetic…
Cellular senescence, a state of permanent growth arrest, has emerged as a hallmark and fundamental driver of organismal aging. It is regulated by both genetic…
Researchers at Yale University and the Broad Institute of MIT and Harvard screened hundreds of millions of cells exposed to the COVID-19 and MERS viruses…
In experiments with rats, pigs and monkeys, Johns Hopkins Medicine researchers have developed a way to deliver sight-saving gene therapy to the retina. If proved…